Methods and Compositions for Treating Lysosomal Storage Disorders
AssigneeSanford Health
InventorsJon Brudvig, Jill Weimer
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Abstract
The present disclosure provides methods and compositions for treating or limiting development of a lysosomal storage disorder, by administering to a subject that has or is at risk of a lysosomal storage disorder thereof an amount effective of a sortilin (SORT1) inhibitor to treat or limit development of the lysosomal storage disorder.
Claims53
A method for treating a lysosomal storage disorder, comprising administering to a subject that has a lysosomal storage disorder thereof an amount effective of a sortilin (SORT1) inhibitor to treat the lysosomal storage disorder.
A method for limiting development of a lysosomal storage disorder, comprising administering to a subject at risk of developing a lysosomal storage disorder an amount effective of a sortilin (SORT1) inhibitor to limit development of the lysosomal storage disorder.
Dependencies are inferred from the claim text.