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US 2019/0160187 A1Published application
Gene therapy for the treatment of aldehyde dehydrogenase deficiency
AssigneesCornell University, Adverum Biotechnologies, Inc.
InventorsMehdi Gasmi, Ronald G. Crystal, Odelya E. Pagovich
Life of this patent
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Abstract
A vector comprising a promoter operably linked to a nucleic acid sequence encoding human aldehyde dehydrogenase, as well as a composition comprising the vector and method of using the vector to treat aldehyde dehydrogenase deficiency, or to prevent or treat a disease characterized by aldehyde dehydrogenase deficiency.
Claims24
A vector comprising a promoter operably linked to a nucleic acid sequence that encodes human aldehyde dehydrogenase.
24-25.(canceled)
Dependencies are inferred from the claim text.