Recombinant human CLN2 protein and methods of its production and use
AssigneeUniversity of Medicine and Dentistry of New Jersey
InventorPeter Lobel
Life of this patent
Estimating the term…
Abstract
The present invention relates to a method for treating a patient having disorder characterized by a deficient amount of functional CLN2 protein in the affected cells, which comprises administering to the patient an amount of CLN2 protein effective to reduce or eliminate the symptoms caused by the deficiency in CLN2 protein.
Claims15
A method for treating a patient having disorder characterized by a deficient amount of functional CLN2 protein in the affected cells, which comprises administering to the patient an amount of CLN2 protein effective to reduce or eliminate the symptoms caused by the deficiency in CLN2 protein.
A method of claim I wherein the disorder is characterized by accumulation of one or more storage products in the lysosomes of the affected cells.
Dependencies are inferred from the claim text.