Compounds for the treatment of glycogen storage disorders
AssigneesHadasit Medical Research Services and Development Ltd., Ramot at Tel-Aviv University Ltd.
InventorsOr Kakhlon, Miguel Enrique Weil, Leonardo Javier Solmesky
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Abstract
Compounds represented by general Formulae I to IV as described herein are disclosed. Further disclosed are composition utilizing the herein disclosed compounds and using the same for the treatment of glycogen storage disorders.
Claims10
A method of treating a medical condition associated with accumulation of polyglucosan bodies in a tissue of a subject, the method comprising administering to the subject a pharmaceutical composition comprising a therapeutically effective amount of a compound
- or a pharmaceutically acceptable salt thereof.
A method of treating a medical condition selected from Adult polyglucosan body disease (APBD), Andersen disease, Forbes disease, and Danon disease, the method comprising administering to the subject a pharmaceutical composition comprising a therapeutically effective amount of a compound
- or a pharmaceutically acceptable salt thereof.
A pharmaceutical composition comprising a therapeutically effective amount of a compound
- or a pharmaceutically acceptable salt thereof, and a pharmaceutically acceptable carrier.
Dependencies are inferred from the claim text.