Back to results
US 11,452,749 B2Granted
Means and methods for AAV gene therapy in humans
AssigneeuniQure IP B.V.
InventorsBart Antonius Nijmeijer, Valerie Ferreira
Life of this patent
Estimating the term…
Abstract
The present invention relates to means and method for AAV based gene therapies in humans. In particular, the present invention relates to the treatment of human patients that may be suspected to have antibodies directed against the AAV intended for use in the treatment.
Claims10
A method of treating a human disease comprising administering an effective amount of an AAV5 gene therapy vector to a human in need thereof;
- wherein the human is not subjected to a pre-screening with an assay to determine anti-AAV5 antibodies;
- and wherein the human has not been subjected to a medical treatment with an AAV5 gene therapy vector prior to the medical treatment.
Dependencies are inferred from the claim text.